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Ask the Expert with Dr. Anna Pakula
Apr 15, 2018
Recent grant recipient Dr. Anna Pakula discusses her work.
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Getting the Kids Back on the Playground
Apr 10, 2018
Text of Lukas Kostka speech given at January Auction.
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From Passive to Active
Mar 19, 2018
ENMC 25th anniversary summit - The Patient Role in Shared Decision Making.
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Spring RFP
Feb 7, 2018
Spring 2018 Request for Research Proposals.
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Research Presentation Slides
Feb 1, 2018
Slide decks for Dr. Tapscott & Dr. Wang from the 27-Jan presentations.
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Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD
Jan 17, 2018
A publication from Scott Harper's lab reporting on the use of an AAV vector to test the safety of two miRNAs in silencing DUX4.
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A Royal Affair
Jan 4, 2018
Annual Auction for FSHD. NEW RENTON LOCATION.
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Progress Update: 3rd Gen Oligonucleotide Targeting DUX4 in Mouse Model
Jan 1, 2018
Yi-Wen Chen DMV PhD provides an update on investigating 3rd generation oligonucleotides.
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Progress Update: Utilization of cell-free DNA as a biomarker
Dec 31, 2017
Initial progress update provided by Premi Haynes PhD.
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MRI change metrics of facioscapulohumeral muscular dystrophy: STIR and T1
Dec 16, 2017
Follow-on publication for previously funded grant.
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Progress Update: Defining the role of post-translational modification on FSHD protein DUX4
Dec 15, 2017
Jocelyn Eidahl, Post-Doctoral Scientist at Nationwide Children’s Hospital provides a progress update.
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Progress Update: Histochemical and morphometric analysis of FSHD biceps
Dec 14, 2017
Final progress update from Dr. Wagner.
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Wellstone Research Update
Nov 28, 2017
A discussion on recent research advances at the Hyatt prior to the Annual Auction.
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Giving Tuesday 2017
Nov 27, 2017
Have your Giving Tuesday donations matched through facebook and The Gates Foundation.
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FSHD Research Funding Overview 2016
Nov 21, 2017
Reporting on worldwide funding of FSHD research.
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Chronic Pain in FSHD
Nov 20, 2017
Chronic Pain Has a Strong Impact on Quality of Life in FSHD.
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Progress Update: Xenograft Mouse Model
Nov 15, 2017
Dr. Bloch provides a brief update of his progress on a xenograft mouse model.
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Keep Calm - It's Raffle Time!
Nov 10, 2017
Pre-Auction Table Captain/Sponsor Raffle
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Scott Harper at Science Week
Nov 8, 2017
Scott Q. Harper, PhD presents emerging molecular therapies for FSHD at FSHD Global event.
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Emerging Molecular Therapies for FSHD
Oct 26, 2017
Scott Q Harper, PhD reviews work at his lab at Nationwide Children's Hospital.