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Update: Candidate biomarkers and modifiers of disease progression
Jun 4, 2026
Update from the Tapscott lab on viral-like particles.
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Progress Update: Discovery of direct DUX4 inhibitors using AI-guided covalent chemistry and high-scale proteomics
Jun 4, 2026
Final report on development of Talus Bio's drug screening technology.
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Update: Molecular Markers of FSHD
May 8, 2026
Development of an animal model that recapitulates the progression of FSHD in humans, and possible activity of T & B Cells.
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Report: Assessing biological activity and in vivo efficiency of the epigenetic activator, 3R-ON
May 8, 2026
Histone Therapeutics is making progress with 3R-ON technology.
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Update: Motor Outcomes to Validate Evaluations in FSHD
Apr 24, 2026
Latest MOVE FSHD Study update.
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Report: Mapping FSHD through single nuclei RNA sequencing
Jan 30, 2026
Final project report.
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Update: Spatial Transcriptomics in FSHD Skeletal Muscle
Dec 19, 2025
Initial update on research progress.
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Report: Assessing biological activity and in vivo efficiency of the epigenetic activator, 3R-ON
Dec 3, 2025
Initial update in this multi-year grant.
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Altay Therapeutics Receives Orphan Drug Designationfor DX5057
Dec 3, 2025
Early investment by Friends pays off.
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Update: Validation of extracellular vesicle-associated circulating biomarkers for FSHD in cross-sectional and longitudinal clinical studies
Nov 23, 2025
Final report on this project.
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Update: Development of advanced human preclinical models for FSHD modeling
Nov 23, 2025
Initial report on creating skeletal muscle models.
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Update: Candidate biomarkers and modifiers of disease progression
Nov 23, 2025
The initial report on this multi-year project.
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Update: Molecular Markers of FSHD
Nov 23, 2025
Latest update on this multi-year project.
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Update: Consequence of Human Satellite II repeat expression in FSHD
Nov 13, 2025
Initial project update.
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Update: Motor Outcomes to Validate Evaluations in FSHD
Aug 26, 2025
Final project report.
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Update: A silencing reporter system to discover factors and pathways implicated in D4Z4 repression in Facioscapulohumeral dystrophy
Aug 22, 2025
Final project report.
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Update: FSHD Blood Biomarker Development
May 25, 2025
One year update.
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Report: Molecular Markers of FSHD
May 3, 2025
Updates on Aim 1 & 2 during year 2.
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Report: The role of macrophages in Facioscapulohumeral muscular dystrophy
Apr 27, 2025
First year report.
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Report: Mapping Facioscapulohumeral muscular dystrophy through single nuclei RNA sequencing
Apr 10, 2025
Year one report on progress.