Search Results
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Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD
Jan 17, 2018, 9:47 PM
A publication from Scott Harper's lab reporting on the use of an AAV vector to test the safety of two miRNAs in silencing DUX4.
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Therapy Q&A
May 1, 2017, 3:40 PM
Interview of Dr. Joel Chamberlain regarding her lab's work on therapy development.